ELRIG, a not-for-profit, volunteer-led organisation dedicated to the global drug discovery community, today announced the ...

While a majority of the therapies currently in development are life-long treatments, Genespire is taking a different approach ...

At a Food and Drug Administration cell and gene therapy (CGT) roundtable last June, most speakers pushed for the agency to ...

Few companies stand better poised than Beam Therapeutics to reap the first fruits of the FDA’s promised flexibility toward ...

Tenaya Therapeutics recently outlined its 2026 priorities, including updates on its TN-201 and TN-401 cardiac gene therapy programs and the resumption of patient enrollment in key Phase 1b/2 trials ...

Clinical and commercial quality controls are eased as the FDA looks to expedite therapy approvals in areas of unmet need.

Nanoscope Therapeutics has received Pioneering Regenerative Medical Product (Sakigake) and Orphan Drug designations for ...

Neurodegenerative diseases (NDDs) represent a profound challenge to global health, characterized by progressive neuronal dysfunction and loss, leading to ...

NHS Scotland has approved a one-time CRISPR gene therapy for severe sickle cell disease, offering durable reduction in ...

Scientists from UC Davis Center for Surgical Bioengineering, the MIND Institute and UC Berkeley’s Murthy Lab are developing ...

This virtual event is part of the Transforming Pediatric Healthcare series from U.S. News & World Report, developed with ...

For those born with certain types of congenital deafness, the cochlear implant has been a positive and enabling technology.